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Blind regain some sight with genes

A new gene therapy has restored some sight in people born with an inherited, progressive form of blindness. The technique replaces a defective gene in the eye with a normal working copy of the gene using a single injection.   The researchers say the findings of this phase 1 trial, published in The Lancet, support the further development of this state-of-the-art treatment for other more common genetic causes of blindness, including degenerative diseases of old age and inherited defects like retinitis pigmentosa. Choroideremia is caused by a mutation in the CHM gene on the X chromosome and affects an estimated…